In a medical milestone that sounds like science fiction, doctors have successfully edited a baby's genes inside the body to treat a rare and deadly genetic disease—marking the first time such a personalized approach has been used in a human being.

The scientific paper titled "Model-guided design of microRNA-based gene circuits supports precise dosage of transgenic cargoes into diverse primary cells" introduces an innovative approach to gene therapy, aiming to ensure that therapeutic genes are expressed at optimal levels within cells.